5 Pharmaceutical preparations, lipids, lipid nanoparticles, lipid formulations, nucleic acid molecules, enzymes, polypeptides, and compounds/agents for medical use; pharmaceutical preparations and therapeutic agents, namely, for RNA, gene therapy and mRNA regulation; pharmaceutical and biological preparations for medical use for the treatment of genetic and genomic disorders by gene therapy and mRNA regulation for use in human and animal therapeutics; pharmaceutical preparations, namely, therapeutic pharmaceuticals developed through genome modifications for the prevention and treatment of genomic disorders in humans and animals; pharmaceutical preparations for gene therapy and mRNA regulation