5 Pharmaceutical, therapeutic pharmaceuticals, and biopharmaceutical preparations and agents for the treatment of a variety of human and animal diseases and disorders, namely, autoimmune diseases and disorders, cardiovascular diseases and disorders, connective tissues diseases and disorders, dermatological diseases and disorders, enzyme deficiency diseases and disorders, gastrointestinal diseases and disorders, genetic diseases and disorders, genitourinary diseases and disorders, hematological diseases and disorders, immunoregulatory diseases and disorders, infectious diseases and disorders, inflammatory diseases and disorders, hepatic diseases and disorders, metabolic diseases and disorders, muscular diseases and disorders, neurological diseases and disorders, neuromuscular diseases and disorders, oncological diseases and disorders, ophthalmological diseases and disorders, rare diseases and disorders, renal diseases and disorders, reproductive disease and disorders, and respiratory diseases and disorders; nucleic acid-based therapeutic pharmaceuticals and therapeutic agents for the treatment of a variety of human and animal diseases and disorders, namely, autoimmune diseases and disorders, cardiovascular diseases and disorders, connective tissues diseases and disorders, dermatological diseases and disorders, enzyme deficiency diseases and disorders, gastrointestinal diseases and disorders, genetic diseases and disorders, genitourinary diseases and disorders, hematological diseases and disorders, immunoregulatory diseases and disorders, infectious diseases and disorders, inflammatory diseases and disorders, hepatic diseases and disorders, metabolic diseases and disorders, muscular diseases and disorders, neurological diseases and disorders, neuromuscular diseases and disorders, oncological diseases and disorders, ophthalmological diseases and disorders, rare diseases and disorders, renal diseases and disorders, reproductive disease and disorders, and respiratory diseases and disorders; chemicals for use in therapeutic product development and manufacturing processes in the medical field